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Cat No. | Product Name | Synonyms | Targets |
---|---|---|---|
T12718L | RG7800 | RO6885247 | Others , DNA/RNA Synthesis |
RG7800 (RO6885247) has the potential for spinal muscular atrophy treatment. RG7800 is an SMN2 splicing modifier. | |||
T12718 | RG7800 hydrochloride (1449598-06-4 free base) | RO6885247 hydrochloride,RG7800 hydrochloride | Others |
RG7800 hydrochloride is an orally active modulator of SMN2 splicing. | |||
T78046 | RG7800 tetrahydrochloride | RO6885247 tetrahydrochloride | DNA/RNA Synthesis |
RG7800 hydrochloride is an orally active modulator of SMN2 splicing, exhibiting EC50 values of 23 nM for SMN2 splicing and 87 nM for SMN protein production. This compound holds promise as a therapeutic agent for spinal m... | |||
T64288 | RG7800 hydrochloride | ||
RG7800 hydrochloride is an orally active SMN2 splicing modulator that acts on SMN2 splicing (EC1.5x: 23 nM) and SMN proteins (EC1.5x: 87 nM). |