2
Cat No. | Product Name | Synonyms | Targets |
---|---|---|---|
T12718L | RG7800 | RO6885247 | Others , DNA/RNA Synthesis |
RG7800 (RO6885247) has the potential for spinal muscular atrophy treatment. RG7800 is an SMN2 splicing modifier. | |||
T12718 | RG7800 hydrochloride (1449598-06-4 free base) | RO6885247 hydrochloride,RG7800 hydrochloride | Others |
RG7800 hydrochloride is an orally active modulator of SMN2 splicing. |